Amicus Therapeutics Inc
A biotechnology company that makes treatments for rare genetic diseases. Its best-known product, Galafold, is an oral pill that helps people with Fabry disease, a condition that damages organs; it also developed a therapy for Pompe disease. Founded in 2002, Amicus traces its start to John Crowley, a father who entered biotech to find a treatment after two of his children were diagnosed with Pompe disease — a story that inspired the 2010 film "Extraordinary Measures." Its name, Amicus, is Latin for "friend," a nod to its collaborative work with patients.